Building In Vivo Pharmacology For Targeting ABCA4 to the Retina Using a Novel Non-viral DNA/Delivery Approach

Time: 11:30 am
day: Day Two Track A - Morning


  • Discuss Intergalactic’s non-viral gene therapy platform for ocular indications
  • Discuss strategy for retina in vivo pharmacology studies using large animal species
  • Demonstrate delivery of the target gene to the relevant cell type in the retina
  • Assess the impact of the delivery method on retinal structure