Company: Harvard Medical School
Job title: Assistant Professor of Ophthalmology
Dr. Liu’s research focuses on improving the understanding of the genetic causes and molecular bases of inherited retinal degenerations (IRDs), and developing novel CRISPR/Cas9-based gene editing therapeutic approaches to overcome hurdles of conventional AAV-mediated gene augmentation therapy for treating dominant IRDs and recessive IRDs that are caused by mutations in large genes. In pursuing this, she has been testing and employing a variety of the most cutting-edge gene editing technologies, both in vitro in cell-based model systems and in vivo using a number of animal models. Her research has led to a number of inventions that in the process of seeking patent protection.
Exploring Next-Generation Therapeutics: The Promise of Gene Editing 4:30 pm
• Exploring the use of various gene editing technologies to treat inherited eye diseases • Investigating the unique challenges associated with gene editing compounded with challenges of gene therapy • Discussing recent data highlighting innovations of gene edited gene therapies to treat ophthalmic disordersRead more
day: Day Two